FDA Approves First Muscle-Targeted Therapy for Spinal Muscular Atrophy — What It Means for Neuromuscular Medicine

Published: September 13, 2026 | Category: Drug Approval On September 11, 2026, the FDA approved Isembyld (apitegromab-mstn) — the first and only therapy designed to directly target muscle tissue in spinal muscular atrophy (SMA). Developed by Scholar Rock, it represents…










